Niemann Pick Type-C (NPC) is a fatal rare genetic disease that impacts every cell in the body.  Often called "Childrens's Alzheimers", the disease progresses rapidly from birth, interrupting neurological development as the cells in the brain and nervous system die off.  This incurable disease causes damage that is irreversible and is ultimately fatal.  Most children diagnosed with NPC will not live to be 10 years old without treatment.

Due to the complexity of the disease and inconsistency of disease progresson, NPC kiddos often struggle for years before getting a confirmed diagnosis.  A few experimental treatment have shown to help slow down the rate of progression of the disease if given early enough.  With NPC every day counts. 

We are extremely blessed to have learned Liam's diagnosis early and we are grateful there is a strong international community established around NPC.